correlation), variability는 다른 얻을수도 o, calculation for AAV rat study,assay power
non-CAD non-phenol Series 5c Discussion on de-prioritizing of TR847: → to make a decision of go/nogo for TR847 by end of September
  • TR847 seems less and less appealing to go ahead for further studies while we have TR084 that shows clean profile.
  • Team should consider to de-prioritize TR847 in this stage based on PK/PD profile, and focus more on TR980 and TR084.
  • TR980 shows comparative potency in BzATP to TR847 and has less concern regarding Br-benzene structure and PK profile.
  • In short term, TR980 would be more challenging because it shows less exposure than TR847.
  • TR084 may show better exposure than TR980, and better profile than TR847 whose T1/2 could not be calculated.
  • If we drop TR847 we go for AAV model with TR980. Meanwhile model is established based on BzATP and TH and PK data.
  • If some of the data does not support for TR084, it drops. Team will make decision on which compound to go CS before CN. CN3 is planned in Feb
  • We will have more discussion if we stop TR847 by next week, but currently TR847 related studies should be pending.
  • Critical data is DSRE cardiomyocyte assay data which is currently repeated and data will be available around end of Sep. (Cardiomyocyteassay data of TR084.)
TH WB - TH IHC - DAT ARG - DATscan - VMAT2 PET TSPO WB - TSPO PET
Series 3 non-CAD

CNS BM, Pathogenic, priority, AAV aSyn rat, → CSF (Oct), ,

TSPO WBTSPO IHCTSPO ARG [3H]PBR-28TSPO PET
Rat AAV-asyn Tentative Study Design Readoutip LPS ratCortex
VMAT2 WBVMAT2 IHCVMAT2 ARGVMAT2 PET ([18F]AV-133)
Rat AAV-asyn Tentative Study Design Readout (tentative) - Before PDE: TH WB (striatum) → DAT OD (striatum)
- After PDE: {Molinet-Dronda, 2015 #2364} unilateral and bilateral 6OHDA RAT longitudinal in-vivo study, Striatum
(Sossi et al. 2022, PMID 35524682) aSyn PFF rat
DAT OD vs DATscan

In vivo

Animal modelTau P301L (=rTg4510 일걸) at ReMynd
Txsystemic LPS vs local BzATP
ReadTau and inflammation

NBB (project number: 1513)

02210 5 tissue advisory board (TAB) discussed and approved your application. reserved all of the available samples. on tab1
https://mytakeda-my.sharepoint.com/:x:/r/personal/jae-won_lee_takeda_com/Documents/NLRP3%20inhibitor/AD/NBB/sample%20selection/1513_Selection_01b.xlsx?d=w4962aba899c04fe58fe6937e5a1a2bfd&csf=1&web=1&e=JqaaQX

50 csf samples of AD donors (frozen samples)
21 plasma samples of AD donors (frozen samples)
17 hippocampal samples of AD donors (frozen samples)
42 hippocampal samples of AD donors (paraffin embedded)

s.i.c.c? Dementia with Senile Involutive Cortical Changes (DEM-SICC), in which the pathology resembles AD, but does not qualify according to all neuropathological criteria.

38 csf samples of dementia donors (frozen samples)
22 plasma samples of dementia donors (frozen samples)
27 hippocampal samples of dementia donors (frozen samples)
35 hippocampal samples of dementia donors (paraffin embedded)

50 csf samples of control donors (frozen samples)
6 plasma samples of control donors (frozen samples)
6 hippocampal samples of control donors (frozen samples)
21 hippocampal samples of control donors (paraffin embedded)

Assays of pyroptosis

Human CSFHuman bloodPBMC
rogliaIBA-1
P3(Luo, 2019 #1852) control n=16, 33.9y, (0.92 ± 0.45 ng/ml)(Chatterjee, 2020 #1263) IN pd, iMark Microplate Reader, BIORAD, USA.(Fan, 2020 #657)
(Peng, 2019 #1853) control n=26, 38.8, 대략 <1 ng/ml)Havrda MSD: detection range from 0.78 ng/mL (Sebastian call this LLOQ),
16.2+ ng/mL (%) — 90th percentile
• None in PD
ab253423, detection &capture antibody, both rraised against [Sebastian] ELISA: Cusabio ELISA (CSB E15885h) (The capture antibody is mouse monoclonal and the detection antibody is goat polyclonal.) Sensitivity (LLOQ) : 0.039 ng/mL
Detection Range : 0.156 ng/mL-10 ng/mL

CRO: RayBiotech
N-term fragment? 20220302: detected from 0.141 (ng/mL) js:거의 광고대로 됐네.어쨌건 Havrda's MSD보단 better 인 듯., NLRP3 in CSF could not be detected. NLRP3 in plasma was detectable but the dilution linearity did not meet the criteria.

MSD: Antibody pair from abcam ELISA kit was used to develop MSD NLRP3 assay. However, as S/B ratio even at 60 ng/mL was as low as 3.3

[SMCxPro]: antibody pair (ab253423, abcam, produced by immunization with N-term fragment), full-length recombinant NLRP3 protein (ab165022, abcam, epitope unknown),
20220428:
-buffer: LLOQ of 44 pg/mL(S/B ratio at 60 ng/mL was dramatically increased to 829, (250-fold higher value than that in MSD)
-CSF: 0.17 ng/mL, couldn't get MRD because all diluted samples were below LLOD (ie no linearity, why?)
-plasma: 4.45 ng/mL, MRD=2
- in both CSF & plasma: spke-recovery was low (~25%),
Issues: low recovery (CSF & plasma), no MRD set up (CSF)
where is the epitope in the full-length recombinant protein (for our standard and spike-in) and Abcam's NLRP3 ELISA's N-term fragment?
Js: 다음 조건 충족이 중요할 것
-High S/B ratio in HC

Uncertain Spans

locationtranscriptionuncertainty
Top header row “correlation), variability는…“partial leftover from previous-page tableTop row appears to be the tail of a planning-table column from the previous capture; reading order is preserved as-seen.
TSPO WB / IHC / ARG / PET cellsinline scatter plots and box plotsPlots are kept as evidence; numeric data points and group-label text inside each plot are below the legible threshold.
VMAT2 ARG plot panel C”p < 0.0001, R² = 0.8251” with axis labels DAT Intensity vs BPNDAxis tick labels (e.g. 6×10⁶) are partially blurred; numeric values preserved as best-effort.
Series 5c bullet list”If we drop TR847 we go for AAV model with TR980. Meanwhile model is established based on BzATP and TH and PK data.”Tail of the line (“Meanwhile model is established”) may continue beyond the visible cell width.