PARKN GT (Takeshi Hioki, PFR-4249-100)

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20240722_182043PARKN GT (Takeshi Hioki, PFR-4249-100) > NHP Studies > Bioanalytical method to differentiate human and monkey ParkinBioanalytical Method To Differentiate Human And Monkey Parkin; Bioanalytical method to differentiate human and monkey Parkin,; Uncertain Spans
20240722_182046PARKN GT (Takeshi Hioki, PFR-4249-100) > NHP Studies > Bioanalytical method to differentiate human and monkey ParkinBioanalytical Method (continued) / NSRB / PRC Narrative / Natural Hx / Population Analysis / Quantitative BM Criteria; Post-PE; Population analysis; MJFF GGPD Project - Subjects; Quantitave BM criteria:; …
20240722_182050PARKN GT (Takeshi Hioki, PFR-4249-100) > Natural Hx study > Quantitative BM criteria / Target validationQuantitative BM Criteria, 20220119 / 20220130 Drafts, And Target Validation Plan; Quantitave BM criteria:; Target validation / Postmortem plan; Questions / Needs / criteria / timeline
20240722_182053PARKN GT (Takeshi Hioki, PFR-4249-100) > PE > PETTarget Validation (continued), PE I Planning, Parkin Binding Assay HTS History, And 20210709 11-Candidate List; Questions / Needs / criteria / timeline; PE I; Parkin Binding Assay / HTS history; 20210615 row; …
20240722_182057PARKN GT (Takeshi Hioki, PFR-4249-100) > PE > PETParkin Binding Assay Development Log (20210615 → 20220715); 20211105 — ASMS results; 20211118; 20211217 — MAKOTO; 20220106 — makoto; …
20240722_182100PARKN GT (Takeshi Hioki, PFR-4249-100) > PE > PETParkin Binding Assay Termination Memo, Controversial Binders, And Start Of PE I Imaging GBA Plan; 20221215 — ADDP E000-25157 [parkin binding assay development]; 20230331_ADDP — ASMS assay development result_E000-5157.pdf; summary and next actions; Next actions (to be discussed); …
20240722_182103PARKN GT (Takeshi Hioki, PFR-4249-100) > RD DDU’s PET Imaging GBA > PK/PD StrategyRDDU’s PE I Imaging GBA Plan (continued), PK/PD Strategy, 20201007 / 2021005 DMPK Meetings, AAV/PK Rationale, PRC1 Parkin Team Considerations, And [Benchmark] FA GT PRC1 PE Narrative; PK/PD Strategy; PRC1; [Benchmark] Molecular biomarker development of FA GT PRC1 PE Narrative; Uncertain Spans
20240722_182106PARKN GT (Takeshi Hioki, PFR-4249-100) > Safety > SharefolderScenario / Disease-Model Questions, Safety De-Risking Strategy, Sharefolder, Parkin Protein Notes, And Assays Table; Safety; Sharefolder; Timeline; Resources: my PGRN in this document; …
20240722_182110PARKN GT (Takeshi Hioki, PFR-4249-100) > TM > AssaysTeam Meetings / Update Meeting To Ceri Links, TM Assays Summary, NBB LLOQ Tables, Brain/CSF Comparison, pS65-Ub Reagents, Ubiquitin Linkage, IVC, And Start Of Parkin Activity Assay; Timeline; Resources: my PGRN in this document; TM Assays; pS65-Ub assays; …